Cellular and Integrative Physiology Seminar Series - Guangping Gao, PhD

Title: Gene Therapy for Rare Diseases: Moving from fundamental to translational science

Summary: My research has primarily focused on molecular genetics and viral vector gene therapy of rare genetic diseases. This encompasses disease gene cloning, causative mutation identification, pathomechanism investigation, animal modeling, novel viral vector discovery and engineering for in vivo gene delivery, vector biology, preclinical and clinical gene therapy product development, viral vector manufacturing for preclinical and clinical gene therapy applications and technology platforms development as novel approaches for human gene therapy.